What Is Milo Biotechnology?

Milo Biotechnology is company developing a therapy that increases muscle strength or decrease the rate of muscle atrophy for the treatment of muscular disorders.

The company’s technology, a gene therapy-based up-regulation of the muscle-strengthening follistatin protein, was developed at and is exclusively licensed from Nationwide Children’s Hospital (Ohio, U.S.A.).

In 2014 the therapy completed a Phase I/II clinical study in Becker Muscular Dystrophy establishing initial safety and efficacy.

Recent News


Milo Biotechnology’s Follistatin Gene Therapy Increases Function in Becker Muscular Dystrophy Patients

Data published today in the journal Molecular Therapy demonstrates initial clinical proof of principle of a gene therapy to increase... Read More →

Preliminary Findings in Milo Follistatin Gene Transfer Study Promising

Preliminary results from a trial to test the safety of injecting follistatin genes into the thigh muscles of adults with... Read More →
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